StudyFinder
A Phase 3, Randomized, Open-label, Parallel-arm, Active-controlled, Multicenter Study to Evaluate Safety and Efficacy of ALXN1850 Versus Asfotase Alfa Administered Subcutaneously in Pediatric (2 to < 12 years of age) Participants with Hypophosphatasia (HPP) Previously Treated with Asfotase Alfa
Status: Recruiting
This is a study to evaluate the safety and efficacy of ALXN1850 in pediatric participants with hypophosphatasia who have been treated with asfotase alfa for at least 6 months.
Sex: Male or Female
Age Group: Up to 18 years old
Inclusion Criteria:
• 2 to 11 years old
• diagnosis of Hypophosphatasia (HPP)
• treated with 6 mg/kg/ week of asfotase alfa via subcutaneous injection administered as either 2mg/kg 3 times per week or 1 mg/kg 6 times per week for at least 6 months
Exclusion Criteria:
• primary or secondary hyperparathyroidism
• hypoparathyroidism, unless secondary to HPP
• any new fracture within past 12 weeks
• body weight less than 10 kg (22 pounds)
Conditions:
Children's Health, Rare Diseases
Keywords:
HPP, Hypophosphatasia
Study Contact: Kyriakie Sarafoglou - saraf010@umn.edu
Principal Investigator: Kyriakie Sarafoglou
IRB Number: STUDY00020817