StudyFinder
A multicenter, single-arm, open label trial to evaluate efficacy and safety of oral, twice daily LNP023 in adult atypical hemolytic uremic syndrome (aHUS) patients who are naive to complement inhibitor therapy
Recruiting
To evaluate the efficacy and safety of iptacopan at a dose of 200 mg twice a day for 52 weeks in patients with atypical hemolytic uremic syndrome (aHUS).
Male or Female
18 years and over
Inclusion Criteria:
• at least 18 years old
• evidence of active Thrombotic Microangiopathy (TMA)
Exclusion Criteria:
• previous or ongoing treatment with complement inhibitors, including anti-C5 antibody
• ADAMTS13 deficiency
• positive test for Shiga toxin * direct Coombs test
• had a bone marrow transplant or hematopoietic stem cell transplant, or a heart, lung, small bowel, pancreas or live transplant
Blood Disorders, Kidney, Prostate & Urinary, Rare Diseases
Clinics and Surgery Center (CSC)
Nattawat Klomjit - klomj001@umn.edu
Nattawat Klomjit
PHASE3
STUDY00020503
See this study on ClinicalTrials.gov